Background

  • Master Protocol types
    • Basket trial
    • Umbrella trial
    • Platform (complex) trial
  • FDA issued oncology master protocol guidance
  • EU/UK published white paper on platform trials and complex designs
  • Different types of master protocol designs, more prominently basket and platform trials, have been implemented in cancer research, started more in exploratory phase and now including confirmatory phase
  • In order to achieve efficiency gain, frequentist and Bayesian statistical approaches have been developed
  • Operational considerations in master protocol implementation seems to be one of the biggest challenges, along with knowledge gap and regulatory interaction complexity

Mission

  • Understand the current regulatory landscape in oncology master protocol designs
  • Assess different master protocol trial designs in different settings (e.g. exploratory vs. confirmatory) to guide implementation and statistical methods
  • Educate and outreach to other functions to resolve knowledge gaps, also develop practice guidance of master protocols

Members

Name Company
   

Projects

  • Learning from FDA master protocol guidance documents for oncology drugs and COVID-19 treatments: similarities and differences
  • White papers on master protocol implementation guide and case example reviews
  • Conference session proposals